Aqneursa has been approved to treat neurological symptoms associated with NPC in children and adults who weigh at least 15kg, ...
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What would the Presidents Cup look like with LIV Players involved? Brooks, Bryson, Niemann, Cam Smith? Maybe not as different ...
Parents pushed for years for treatments for the neuron disease Niemann-Pick type C. After setbacks, one drug now has FDA ...
With two drugs cleared by the U.S. FDA for Niemann-Pick disease type C (NPC) in less than seven days, Wall Street was ...
The FDA gave the green light to levacetylleucine (Aqneursa) as a stand-alone treatment for Niemann-Pick disease type C (NPC), ...
Find covers, cartoons, and more at the Condé Nast Store. In the weeks before John Wayne Gacy’s scheduled execution, he was ...
Miplyffa treats Niemann-Pick disease type C, which progressively impacts the abilities to speak, swallow, and walk or move ...
While it was just last week that Zevra Therapeutics’ Miplyffa became the first FDA-approved treatment for the lysosomal ...
The small molecule drug arimoclomol (Miplyffa) has got the green light from the U.S. Food and Drug Administration (FDA) for ...
IntraBio’s Aqneursa is the second drug within a week approved by the regulator for treating Niemann-Pick disease type C, just ...
The Food and Drug Administration (FDA) has approved Aqneursa ™ (levacetylleucine) for the treatment of neurological manifestations of Niemann-Pick disease type C (NPC) in adult and pediatric patients ...